Sickle cell disease occurs when a child inherits two sickle cell genes—one from each parent. Lillian knew she carried the ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

Gene-editing tools like CRISPR are being used to cure people of sickle cell anemia and other diseases with gene therapy.

Genes are made of DNA (deoxyribonucleic acid) that contains instructions for making proteins. Proteins are incredibly important in cells as they carry out essential functions necessary for cell ...

UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

Cyclosporin H boosts a new lentivirus-delivered gene therapy with enhanced anti-sickling properties in blood stem cells from ...

Wilson celebrates the first U.S. patient to complete gene therapy for sickle cell, but says advocacy must continue.

They can also predispose you to certain diseases. Thousands of diseases — such as cystic fibrosis, sickle cell anemia and cancer — are caused when there’s a change or mutation in a gene. Most people ...

The amino acid glutamine plays an unexpected role in erythropoiesis, the differentiation of erythroid progenitor cells into ...

MEMPHIS, Tenn. - November 14, 2024) Blood stem cells develop through different stages to become fully mature red blood cells. This fundamental ...

Blood stem cells develop through different stages to become fully mature red blood cells. This fundamental biologic process ...

Q3 2024 Earnings Call Transcript November 13, 2024 Operator: Good morning, and welcome to Fulcrum Therapeutics Third Quarter ...