9-case cluster of rare pneumonia being investigated by Gaston County health officials
Public health officials are investigating a cluster of nine confirmed cases of Legionnaires’ disease among people who ...
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Woman with rare disease claims she’s now blind and bruised after doctors made her get 3 vaccines
A 23-year-old Florida woman has been temporarily blinded and bruised after allegedly being required to receive multiple ...
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After prior snub, Zevra clinches FDA approval for rare lysosomal storage disorder drug Miplyffa
For Zevra Therapeutics and its rare neurodegenerative disease med arimoclomol, the second time’s the charm. | The ...
US FDA approves Zevra's treatment for rare genetic disease
The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...
FDA Approves Zevra's Miplyffa for Niemann-Pick Disease Type C — 2nd Update
Zevra Therapeutics has won Food and Drug Administration approval of Miplyffa for Niemann-Pick disease type C, or NPC, making it the first drug cleared in the U.S. for the rare neurodegenerative ...
Voucher program notches win as clock ticks
The FDA’s priority review voucher program for rare pediatric diseases is set to lapse on Sept. 30 without congressional intervention.
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FDA ap­proves Zevra’s rare dis­ease drug af­ter re­sub­mis­sion
After a second review, the FDA approved Zevra Therapeutics’ treatment for Niemann-Pick disease type C, a progressive rare ...
Understanding rabies in dogs: Symptoms, treatment and prevention
Rabies is a viral disease transmitted through the saliva of infected animals such as dogs, bats, and raccoons. It affects the ...
Vaccine horror as woman, 23, left ‘temporarily blind with agonising bruises engulfing her face’
A WOMAN claims she was left temporarily blind with agonising purple bruises spreading across her face after having three ...
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Calves to Cure helps fund research for Worden boy's rare disease
The Billings Livestock Commission hosted the sixth annual Calves to Cure on Thursday, an event to help raise money and ...