US FDA approves Zevra's treatment for rare genetic disease
The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...
Two more West Nile Virus cases reported in R.I.
There are now two confirmed and two probable cases of the mosquito borne illness and one EEE case in the state ...
Wastewater monitoring can detect foodborne illness, researchers find
First used in the 1940s to monitor for polio, wastewater surveillance proved such a powerful disease monitoring tool that the ...
FDA Approves Zevra's Miplyffa for Niemann-Pick Disease Type C
Zevra Therapeutics has won Food and Drug Administration approval of Miplyffa for Niemann-Pick disease type C, making it the first drug cleared in the U.S. for the rare neurodegenerative disorder.
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Although Gene Therapy Offers Hope, SMA Patients Still Face Significant Health Challenges
Children with spinal muscular atrophy (SMA) experience benefits from receiving a disease-modifying gene therapy, but many ...
I was diagnosed with a stage 4 blood cancer that affects elderly people - but I'm only 16
Alizabeth Rhodes was taken to the ER in her home state with 'non-specific' symptoms at the age of 16 years - which may have ...
YOUR HEALTH: Emmitt’s story: From a head cold to a rare heart condition
An eight-year-old boy’s experience could be your own. He went to the doctor for head cold symptoms. He ended up in the OR to ...